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Story Archive
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Drs. Sylvia Fong & Soumi Gupta Discuss the Significance of AAV Therapies
What’s going on at the cutting edge of gene therapy research? We speak with Drs. Sylvia Fong and Soumi Gupta to find out
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Advancing our understanding of gene therapy research, one publication at a time
澳门正规博彩十大排行平台 recently published data from a phase 3 hemophilia A trial in the New England Journal of Medicine. More details within!
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Meet the Scientist: Christian Vettermann, Ph.D.
In his latest paper, Dr. Vettermann solves a complex problem facing hemophilia A scientists and clinicians for years
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Center of Technology (CoTe)
Our Products
Each of our eight approved therapies reset the standard of care for the conditions they treat.
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Each drug candidate we pursue is guided by a fundamental understanding of the genetics and underlying biology of the condition it will address.
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